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- AAV1/2-CMV/CBA-human-A53T-alpha-SYN AAVGD1001-RVAAV1/2AAV1/2-CMV-CBA-human-A53T-alpha-synuclein-WPRE-BGH......CMV>5x10^12 GC/mL
- AAV1/2-CMV/CBA-Null/Empty AAV virusGD1004-RVAAV1/2AAV1/2-CMV-CBA-Null/Empty-WPRE-BGH-polyACMV>5x10^12 GC/mL